| Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy A Biffi, E Montini, L Lorioli, M Cesani, F Fumagalli, T Plati, C Baldoli, ... Science 341 (6148), 2013 | 1031 | 2013 |
| Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome A Aiuti, L Biasco, S Scaramuzza, F Ferrua, MP Cicalese, C Baricordi, ... Science 341 (6148), 2013 | 935 | 2013 |
| Targeted genome editing in human repopulating haematopoietic stem cells P Genovese, G Schiroli, G Escobar, T Di Tomaso, C Firrito, A Calabria, ... Nature 510 (7504), 235-240, 2014 | 500 | 2014 |
| Targeted genome editing in human repopulating haematopoietic stem cells P Genovese, G Schiroli, G Escobar, T Di Tomaso, C Firrito, A Calabria, ... Nature 510 (7504), 235-240, 2014 | 500 | 2014 |
| Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial M Sessa, L Lorioli, F Fumagalli, S Acquati, D Redaelli, C Baldoli, ... The Lancet 388 (10043), 476-487, 2016 | 256 | 2016 |
| MYO1E mutations and childhood familial focal segmental glomerulosclerosis C Mele, P Iatropoulos, R Donadelli, A Calabria, R Maranta, P Cassis, ... New England Journal of Medicine 365 (4), 295-306, 2011 | 239 | 2011 |
| Genomewide association study using a high-density single nucleotide polymorphism array and case-control design identifies a novel essential hypertension susceptibility locus in … E Salvi, Z Kutalik, N Glorioso, P Benaglio, F Frau, T Kuznetsova, H Arima, ... Hypertension 59 (2), 248-255, 2012 | 149 | 2012 |
| Genomewide association study using a high-density single nucleotide polymorphism array and case-control design identifies a novel essential hypertension susceptibility locus in … E Salvi, Z Kutalik, N Glorioso, P Benaglio, F Frau, T Kuznetsova, H Arima, ... Hypertension 59 (2), 248-255, 2012 | 149 | 2012 |
| Targeted next-generation sequencing appoints c16orf57 as clericuzio-type poikiloderma with neutropenia gene L Volpi, G Roversi, EA Colombo, N Leijsten, D Concolino, A Calabria, ... The American Journal of Human Genetics 86 (1), 72-76, 2010 | 132 | 2010 |
| In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells L Biasco, S Scala, LB Ricci, F Dionisio, C Baricordi, A Calabria, ... Science translational medicine 7 (273), 273ra13-273ra13, 2015 | 109 | 2015 |
| A multilevel data integration resource for breast cancer study E Mosca, R Alfieri, I Merelli, F Viti, A Calabria, L Milanesi BMC systems biology 4 (1), 1-11, 2010 | 95 | 2010 |
| Precise gene editing preserves hematopoietic stem cell function following transient p53-mediated DNA damage response G Schiroli, A Conti, S Ferrari, L Della Volpe, A Jacob, L Albano, S Beretta, ... Cell stem cell 24 (4), 551-565. e8, 2019 | 82 | 2019 |
| Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia S Marktel, S Scaramuzza, MP Cicalese, F Giglio, S Galimberti, ... Nature medicine 25 (2), 234-241, 2019 | 69 | 2019 |
| HIV-1-mediated insertional activation of STAT5B and BACH2 trigger viral reservoir in T regulatory cells D Cesana, FRS de Sio, L Rudilosso, P Gallina, A Calabria, S Beretta, ... Nature communications 8 (1), 1-11, 2017 | 46 | 2017 |
| Safe and efficient gene therapy for pyruvate kinase deficiency M Garcia-Gomez, A Calabria, M Garcia-Bravo, F Benedicenti, P Kosinski, ... Molecular Therapy 24 (7), 1187-1198, 2016 | 36 | 2016 |
| miRNA-126 orchestrates an oncogenic program in B cell precursor acute lymphoblastic leukemia S Nucera, A Giustacchini, F Boccalatte, A Calabria, C Fanciullo, T Plati, ... Cancer cell 29 (6), 905-921, 2016 | 36 | 2016 |
| Immunotherapy of acute leukemia by chimeric antigen receptor-modified lymphocytes using an improved Sleeping Beauty transposon platform CF Magnani, N Turazzi, F Benedicenti, A Calabria, E Tenderini, ... Oncotarget 7 (32), 51581, 2016 | 31 | 2016 |
| Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe‐affected non‐human primates by intracerebral lentiviral gene therapy V Meneghini, A Lattanzi, L Tiradani, G Bravo, F Morena, F Sanvito, ... EMBO molecular medicine 8 (5), 489-510, 2016 | 31 | 2016 |
| Preclinical Testing of the Safety and Tolerability of Lentiviral Vector–Mediated Above-Normal Alpha-L-Iduronidase Expression in Murine and Human Hematopoietic Cells Using … I Visigalli, S Delai, F Ferro, F Cecere, M Vezzoli, F Sanvito, F Chanut, ... Human gene therapy 27 (10), 813-829, 2016 | 29 | 2016 |
| VISPA: a computational pipeline for the identification and analysis of genomic vector integration sites A Calabria, S Leo, F Benedicenti, D Cesana, G Spinozzi, M Orsini, ... Genome medicine 6 (9), 1-12, 2014 | 25 | 2014 |
Luigi NaldiniDirector, SR-TIGET, San Raffaele Telethon Institute for Gene Therapy, Professor of Tissue BiologyBestätigte E-Mail-Adresse bei hsr.it
